New study finds early decline in trunk control among boys with DMD
The ability to keep the torso upright, known as trunk control, might decline even while boys with DMD are still able to walk
News
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Fractures and growth delays remain common in boys with Duchenne
Half of boys with Duchenne muscular dystrophy had vertebral fractures, many of which happened silently without obvious trauma.
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Case report: Infant’s abnormal liver enzymes lead to early DMD diagnosis
Transaminitis with no signs of liver dysfunction may signal DMD long before visible weakness or motor delays present, study suggests.
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Research suggests tracheostomies are often unnecessary for people with DMD
Many patients with DMD can live well into adulthood using continuous noninvasive breathing support combined with cough-assist devices.
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New data suggests del-zota reverses muscle decline in Duchenne
In a one-year trial, del-zota helped boys with DMD gain strength and function, reversing their expected decline.
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Study finds age and steroid use drive bone loss in Duchenne muscular dystrophy
Children with DMD experience steady bone loss as they age and continue steroid treatment, raising concerns for long-term mobility.
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DMD caregivers willing to tolerate risk in the hopes of prolonging ambulation
A survey found that most DMD caregivers would choose a therapy with variable outcomes even if there was a risk of earlier loss of ambulation.
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More awareness needed of uncommon severe comorbidities in DMD
A recent study identified many severe comorbidities in patients with DMD, including gastrointestinal, cardiovascular and kidney conditions.
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New study links growth trajectories to functional outcomes in boys with DMD
Changes in height and weight over time may be closely tied to motor function outcomes in young boys with DMD, research finds
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Experts set standards to guide safer Duchenne gene therapy
The Muscular Dystrophy Association and Parent Project Muscular Dystrophy released guidelines to help safely use gene therapy for DMD.
