Research suggests tracheostomies are often unnecessary for people with DMD
Many patients with DMD can live well into adulthood using continuous noninvasive breathing support combined with cough-assist devices.
News
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New data suggests del-zota reverses muscle decline in Duchenne
In a one-year trial, del-zota helped boys with DMD gain strength and function, reversing their expected decline.
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Study finds age and steroid use drive bone loss in Duchenne muscular dystrophy
Children with DMD experience steady bone loss as they age and continue steroid treatment, raising concerns for long-term mobility.
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DMD caregivers willing to tolerate risk in the hopes of prolonging ambulation
A survey found that most DMD caregivers would choose a therapy with variable outcomes even if there was a risk of earlier loss of ambulation.
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More awareness needed of uncommon severe comorbidities in DMD
A recent study identified many severe comorbidities in patients with DMD, including gastrointestinal, cardiovascular and kidney conditions.
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New study links growth trajectories to functional outcomes in boys with DMD
Changes in height and weight over time may be closely tied to motor function outcomes in young boys with DMD, research finds
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Experts set standards to guide safer Duchenne gene therapy
The Muscular Dystrophy Association and Parent Project Muscular Dystrophy released guidelines to help safely use gene therapy for DMD.
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Eteplirsen delays cardiac decline in DMD clinical trials
A recent study found that individuals with DMD who receive eteplirsen have slower declines in cardiac function than those who do not.
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World Duchenne Awareness Day 2025: How to get involved
World Duchenne Awareness Day takes place on September 7 each year to raise awareness of DMD and advocate for improved research and education.
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Claims study finds costs rapidly increase as DMD progresses
A German health care claims analysis finds that direct and indirect costs for DMD soar as patients progress through the disease stages.
