New research identifies inhibiting EZH2 as potential DMD treatment
A new study found that blocking the protein EZH2 with an inhibitor drug improved muscle health and function in mice with DMD.
News
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New genetic therapy shows promise in improving muscle health in DMD
A new genetic therapy, WVE-N531, has shown promise in improving muscle health in boys with Duchenne muscular dystrophy (DMD).
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Study finds no clear benefit in heart function from starting cardiac drugs early in DMD
Starting heart medications early in boys with Duchenne muscular dystrophy (DMD) did not prevent the heart’s decline over five years.
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Case study examines nighttime ventilation in patients with both DMD and autism
A recent case study shows the challenges of initiating non-invasive ventilation (NIV) in patients with DMD and neurocognitive comorbidities.
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DMD progression found to vary greatly among patients
In Duchenne muscular dystrophy (DMD), the age when symptoms start and how quickly they get worse can be very different from person to person.
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Children with DMD face challenges performing two tasks at once, study finds
Boys with DMD have a harder time doing two things at once than their peers without the disease, negatively affecting everyday life.
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How muscle strength and flexibility shift over time in boys with DMD
Muscle weakness in Duchenne muscular dystrophy (DMD) does not follow a simple decline, but has periods of stability before worsening.
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Study finds endogenous utrophin shows promise as treatment for DMD
Mice studies show that the activation of endogenous utrophin is a promising therapeutic strategy in alleviating DMD symptoms.
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Families and care teams face obstacles to shared decision-making in DMD
The lack of clear information combined with the limited treatments for DMD impact shared decision making between families and providers.
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New study shines light on DMD symptoms in women
A new study suggests that some female carriers of Duchenne muscular dystrophy (DMD) mutations experience symptoms and complications.
