Mexico, likely home to thousands with DMD, lags in recognizing and treating the disease
Advocacy groups in the country are working to establish a Duchenne registry and clinical guidelines.
Advocacy groups in the country are working to establish a Duchenne registry and clinical guidelines.
Raniya and her younger brother were treated with Sarepta’s single-infusion gene therapy in October 2024.
“It’s just a matter of figuring out how to keep using my voice,” Rothe said.
A documentary exploring the life of a World of Warcraft player with DMD has raised awareness of the disease.
Misha and his family fled their home when the war began and now live in Richmond, Virginia.
Motivational speaker and advocate Dan Lier discusses his work helping those with rare diseases find new mindsets after diagnosis.
In his new memoir, Chris Lewis explores his father’s dedication to fighting muscular dystrophy.
The report examines the “dark corners of Duchenne” through conversations with caregivers.
A 16-year-old boy with Duchenne muscular dystrophy (DMD) died of acute liver failure several months after receiving Elevidys, a gene therapy.